2013 Awardees

Fellowship Project Award

Samantha Gouw Samantha Gouw
Emma Children's Hospital, Academic Medical Center, Amsterdam, The Netherlands
Genetic markers of inhibitor development
Mara Malerba Mara Malerba
Fondazione Luigi Villa, Milan, Italy
Burden of osteoporosis study
Grace Monis Grace Monis
University of Washington Medical Center, Seattle, WA, USA
Stem cell therapy for hemophilia
Bobby Duc Tran Bobby Duc Tran
Emory University, Atlanta, GA, USA
Association of adherence to factor replacement therapy with health literacy and numeracy

Early Career Investigator Award

Roger Preston Roger Preston
Trinity College Dublin, Ireland
The role of glycoprotein Ibα in mediating FVIIa therapeutic activity
Federico Mingozzi Federico Mingozzi
Université Pierre et Marie Curie, Paris, France
Novel strategies to circumvent preexisting humoral immunity to AAV vectors
Nikolett Wohner Nikolett Wohner
INSERM, Paris, France
Clearance mechanisms of native and modified activated factor VII
David Markusic David Markusic
University of Florida, FL, USA
Overcoming imunological barriers to AAV gene therapy for hemophilia

Special Project Award

Carl Blobel Carl Blobel
Hospital for Special Surgery, New York, NY, USA
Role of the iRhom2/TACE/TNFα signaling axis in hemophilic arthropathy
Paris Margaritis Paris Margaritis
The Children’s Hospital of Philadelphia, PA, USA
Novel role of the endothelium in the hemostatic action of FVIIa administration in hemophilia
Anne Angelillo-Scherrer Anne Angelillo-Scherrer
University Medical Center and University of Lausanne, Switzerland
Blocking protein S to treat hemophilia in mice
Keiji Nogami Keiji Nogami
Nara Medical University, Kashihara, Japan
A novel regulatory mechanism of factor (F)VIIa/tissue factor associated with FVIII on the initial phase of coagulation

Caregiver Award

Elena Boccalandro Elena Boccalandro
Fondazione Luigi Villa, Milan, Italy
Aging with hemophilia
Cathliyn Buranahirun Cathliyn Buranahirun
Children’s Hospital Los Angeles, CA, USA
Multicultural needs assessment and transition to adult care for adolescent hemophilia patients
Cesar Haddad Cesar Haddad
Lebanese Association For Hemophilia, Beirut, Lebanon
Optimal physiotherapy treatment for Lebanese persons with hemophilia, based on objective measurements
Luz Villalaz Luz Villalaz
Hospital Del Niño, Republica De Panama
Clinics for young people with hemophilia; providing them with valuable tools for the future