2017 Awardees

Fellowship Project Awardees

Doshi Dr Bhavya Doshi
Children’s Hospital of Philadelphia, Philadelphia, PA, USA
Role of anti-BLyS directed therapy in inhibitor eradication
Toenges Dr Rosa Toenges
University Hospital Frankfurt, Goethe University Frankfurt, Frankfurt, Germany
Exploring template-free CRISPR/Cas9 genomic editing for hemophilia A treatment

Early Career Investigator Awardees

Balestra Dr Dario Balestra
University of Ferrara, Ferrara, Italy
F8 splicing-switching molecules for tailored hemophilia A therapies
Basavaraj Dr Manjunath Goolyam Basavaraj
Children’s Hospital of Philadelphia, Philadelphia, PA, USA
Novel strategies to enhance Factor X activation through improved Factor VIIIa cofactor activity and stability
Lee Dr Adrienne Lee
University of Calgary, Calgary, AB, Canada
The role of factor VIII and joint arthropathy in bone density, microarchitecture and bone strength in adolescent severe hemophilia A
Pavani Dr Giulia Pavani
French National Institute of Health and Medical Research, Paris, France
Targeted integration of FVIII in the globin locus for ex vivo gene therapy of hemophilia A
Singer Dr Heike Singer
Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn, Bonn, Germany
Intracellular identification of FVIII from HA-patients with nonsense mutations in relation to their MHC-driven risk for inhibitor formation

Special Project Awardees

Margaritis Dr Paris Margaritis
Children’s Hospital of Philadelphia, Philadelphia, PA, USA
The effects of the EPCR–factor VII/VIIa interaction in normal and hemophilic conditions
Preston Dr Roger Preston
Royal College of Surgeons in Ireland, Dublin, Ireland
Engineered thrombomodulin variants as novel pro-haemostatic agents for haemophilia therapy
Toh Professor Cheng Hock Toh
University of Liverpool, Liverpool, UK
Histone-enhanced prothrombin activation: Unravelling the mechanism for new therapies in hemophilia
Zhang Dr Ai-Hong Zhang
Uniformed Services University of the Health Sciences, Bethesda, MD, USA
BAR regulatory T cell therapy for anti-FVIII inhibitor development

Caregiver Awardees

Sulochana Ms. Sulochana Badagabettu
Manipal College of Nursing, Manipal, India
Explore the bio-psychosocial status (physical symptoms, self-reported anxiety, stress and social support), coping strategies and lived experiences among women carrier for haemophilia: A mixed method approach
Joseph Ms. Cilla Joseph
Hemophilia Treatment Center, District Hospital, Aluva, India
Effectiveness of hydrotherapy along with Ai Chi techniques for arthritic knee joint in hemophilia patients
McCabe Ms. Erin McCabe
Governors of the University of Alberta, Edmonton, AB, Canada
The assessment of therapeutic relationships in hemophilia care

Outcomes Research Awardees

Mancuso Dr Maria Elisa Mancuso
Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
A prospective registry target on critical outcomes in older patients with severe/moderate hemophilia
Resseguier Dr Noémie Resseguier
Assistance Publique Hopitaux de Marseille, Marseille, France
Quality of life and adjustment among siblings of children and adolescents with severe hemophilia